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Autori: Giraldo Pilar

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Naslov Pivotal trial with plant cell-expressed recombinant glucocerebrosidase, taliglucerase alfa, a novel enzyme replacement therapy for Gaucher disease (Erratum - errors in Affiliations - vol 118, pg 5767, 2011) (Correction)
Autori Zimran Ari Brill-Almon Einat Chertkoff Raul Petakov Milan S Blanco-Favela Francisco Munoz Eduardo Terreros Solorio Meza Sergio Eduardo Amato Dominick J Duran Gloria Giona Florina Heitner Rene Rosenbaum Hanna Giraldo Pilar Mehta Atul Park Glen Phillips Mici Elstein Deborah Altarescu Gheona Szleifer Mali Hashmueli Sharon Aviezer David 
Info BLOOD, (2012), vol. 119 br. 19, str. 4577-4577
Ispravka Web of Science   Elečas   Rang časopisa   Citati: Web of Science  
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Naslov Plant Cell Expressed Recombinant Glucocerebrosidase - Taliglucerase alfa as Therapy for Gaucher Disease in Patients Previously Treated with Imiglucerase (Meeting Abstract)
Autori Pastores Gregory M Fernhoff Paul M Szer Jeffrey Petakov Milan S Cox Timothy M Giraldo Pilar Rosenbaum Hanna Amato Dominick J Mengel Eugen Chertkoff Raul Almon-Brill Einat Zimran Ari 
Info MOLECULAR GENETICS AND METABOLISM, (2012), vol. 105 br. 2, str. S50-S50
Ispravka Web of Science   Članak   Elečas   Rang časopisa   Citati: Web of Science  
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Naslov Plant Cell Expressed Recombinant Glucocerebrosidase - taliglucerase alfa - as Therapy for Gaucher Disease in Patients Previously Treated with imiglucerase (Meeting Abstract)
Autori Pastores Gregory M Fernhoff Paul M Szer Jeffrey Petakov Milan S Cox Timothy M Giraldo Pilar Rosenbaum Hanna Amato Dominick J Mengel Eugen Chertkoff Raul Almon-Brill Einat Zimran Ari 
Info MOLECULAR GENETICS AND METABOLISM, (2011), vol. 102 br. 2, str. S33-S33
Ispravka Web of Science   Članak   Elečas   Rang časopisa   Citati: Web of Science  
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Naslov Peripheral neuropathy in adult type 1 Gaucher disease: a 2-year prospective observational study (Article)
Autori Biegstraaten Marieke Mengel Eugen Marodi Laszlo Petakov Milan S Niederau Claus Giraldo Pilar Hughes Derralyn Mrsic Mirando Mehta Atul Hollak Carla EM van Schaik Ivo N 
Info BRAIN, (2010), vol. 133 br. , str. 2909-2919
Projekat European Working Group on Gaucher Disease (EWGGD) ; Actelion Pharmaceuticals Ltd ; Actelion Pharmaceuticals Ltd, Allschwil, Switzerland
Ispravka Web of Science   Članak   Elečas   Rang časopisa   Citati: Web of Science   Scopus  
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Naslov Polyneuropathy in Type 1 Gaucher disease: A two-year, multinational, prospective observational study (Meeting Abstract)
Autori Biegstraaten Marieke Mengel Eugen Marodi Laszlo Petakov Milan S Niederau Claus Giraldo Pilar Hughes Derralyn Mrsic Mirando Mehta Atul Hollak Carla EM van Schaik Ivo N 
Info MOLECULAR GENETICS AND METABOLISM, (2010), vol. 99 br. 2, str. 14-
Ispravka Web of Science   Članak   Elečas   Rang časopisa   Citati: Web of Science  
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Naslov Prevalence of polyneuropathy in adult type 1 Gaucher disease (GD1): A multinational prospective observational study (Meeting Abstract)
Autori Hollak Carla EM Biegstraaten Marieke van Schaik Ivo N Mengel Eugen Marodi Laszlo Petakov Milan S Niederau Claus Giraldo Pilar Hughes Derralyn Mrsic Mirando Mehta Atul 
Info JOURNAL OF INHERITED METABOLIC DISEASE, (2007), vol. 30 br. , Suppl. Suppl. 1 , str. 107 -107
Ispravka Web of Science   Članak   Elečas   Rang časopisa   Citati: Web of Science   Scopus  
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