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Naslov AMFR dysfunction causes autosomal recessive spastic paraplegia in human that is amenable to statin treatment in a preclinical model (Article; Early Access)
Autori Deng Ruizhi ... Capo Ivan Dj  ... (broj koautora 52) 
Info ACTA NEUROPATHOLOGICA, (2023), vol. br. , str. -
Projekat China Scholarship Council (CSC) PhD Fellowship [201906300026, 202008500138]; Stichting 12q; Solve-RD project within the European Rare Disease Models & Mechanisms Network (RDMM-Europe); European Union's Horizon 2020 research and innovation programme; National Institute for Health Research; Wellcome Trust; Cancer Research UK; Medical Research Council; NIHR Manchester Biomedical Research Centre [FCC/1/1976-25]; Spastic Paraplegia Foundation (USA); NHS England; King Salman Center for Disability Research [REI/1/4446-01]; King Abdullah University of Science and Technology (KAUST), Office of Sponsored Research (OSR) [91617021, 09150172110002]; Netherlands Organisation for Scientific Research (ZonMw Veni) [779257]; the Netherlands Organisation for Scientific Research (ZonMw Vidi); Erasmus MC Fellowship 2017; Erasmus MC Human Disease Model Award 2018; [NIHR203308]; [2180-004]
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