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Naslov Redefining triple a syndrome: a multinational study of the neuromuscular phenotype in the largest genetically confirmed cohort to date (Meeting Abstract)
Autori Oeztuerk M Leonard-Louis S De Benito D Natera Nascimento A Ortez C Viric Vanja Stevic Z Nelke C Schaenzer A Previtali S Cehic M Dumic Katja Peric S Roos A Ruck T 
Info NEUROMUSCULAR DISORDERS, (2025), vol. 53 br. , Suppl. S, str. -
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Naslov Short-term and long-term safety profile of Givinostat in Duchenne muscular dystrophy (Meeting Abstract)
Autori Vucinic Dragana M Nascimento A Finkel R Brandsema J Finanger E Harper A Acsadi G Nevo Y Houwen van Opstal S Blaschek A Coceani N Cazzaniga S Bettica P Muelas N 
Info NEUROMUSCULAR DISORDERS, (2024), vol. 43 br. , Suppl. 1, str. -
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